Global Sandhoff Disease Treatment Market is growing at a steady CAGR during the forecast period

Published Date: August 2023

The Sandhoff disease is an exceedingly rare lysosomal storage condition. As a result, nerve cells are damaged (neurodegeneration). This impairs one's ability to think and move. Sandhoff disease, also known as Beta-hexosaminidase-beta-subunit deficiency, is a fatal lysosomal storage disease that causes progressive neuron loss in the brain and spinal cord in children. Abnormalities in the HEXB gene, which is vital for the control of a critical enzyme called beta-hexosaminidase, lead it to accumulate fat called G2 gangliosides. The buildup of cholesterol in nerve cells hinders their function and contributes to other neurological problems.

The report " Global Sandhoff Disease Treatment Market, By Type (Infantile, Juvenile and Late onset), By Treatment (Medication and Surgery), By Therapy (Gene therapy, Enzyme replacement therapy, Stem cell therapy and Others), By End-user (Hospital, Homecare, Specialty Clinics and Others) and By Region (North America, Europe, Asia Pacific, Latin America, and Middle East & Africa) - Market Trends, Analysis, and Forecast till 2030

Key Highlights:

  • Axovant Gene Therapies Ltd published clinical trial data for AXO-AAV-GM2, a gene therapy for Tay-Sachs disease, in March 2019.
  • IntraBio acquired FDA Rare Pediatric Disease designation for IB1001, a new medication for the treatment of GM2 Gangliosidosis, in December 2018. (Tay-Sachs and Sandhoff Disease.

Analyst View:

An increase in public knowledge of hereditary disorders will be a market driver. The emergence of regulatory bodies' special medicine designations is another factor driving market growth. In the foreseeable future, rising biotechnology and pharmaceutical industry R&D spending will also serve as a market. As the competitive landscape among pharmaceutical companies improves, the market is expected to develop. Many pharmaceutical businesses have limited operational income opportunities for focused medicine research and development, which can impede market growth.

 

Browse 60 market data tables* and 35 figures* through 140 slides and in-depth TOC on “Global Sandhoff Disease Treatment Market, By Type (Infantile, Juvenile and Late onset), By Treatment (Medication and Surgery), By Therapy (Gene therapy, Enzyme replacement therapy, Stem cell therapy and Others), By End-user (Hospital, Homecare, Specialty Clinics and Others) and By Region (North America, Europe, Asia Pacific, Latin America, and Middle East & Africa) - Market Trends, Analysis, and Forecast till 2030

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Key Market Insights from the report:

The Global Sandhoff Disease Treatment Market is segmented based on the type, treatment, therapy, end-user, and region.

  • By Type, the Global Sandhoff Disease Treatment Market is segmented into Infantile, Juvenile and Late onset.
  • By Treatment, the market is segmented in Medication and Surgery.
  • By Therapy, the Global Sandhoff Disease Treatment Market is segmented into Gene therapy, Enzyme replacement therapy, Stem cell therapy and Others.
  • By End-User, the market is segmented into Hospital, Homecare, Specialty Clinics and Others.
  • By Region, the Global Sandhoff Disease Treatment Market is segmented into North America, Europe, Asia Pacific, Latin America, and Middle East & Africa. North America is expected to grow significantly in the Global Sandhoff Disease Treatment Market.

Competitive Landscape:

The key players operating in the global Sandhoff Disease Treatment market includes Intrabio, Axovant Gene Therapies Ltd and others. The global Sandhoff disease treatment market is extremely fragmented, and leading competitors have employed a variety of strategies to expand their footprints in this market, including new product releases, expansions, agreements, joint ventures, partnerships, acquisitions, and others.

The market provides detailed information regarding the industrial base, productivity, strengths, manufacturers, and recent trends which will help companies enlarge the businesses and promote financial growth. Furthermore, the report exhibits dynamic factors including segments, sub-segments, regional marketplaces, competition, dominant key players, and market forecasts. In addition, the market includes recent collaborations, mergers, acquisitions, and partnerships along with regulatory frameworks across different regions impacting the market trajectory. Recent technological advances and innovations influencing the global market are included in the report.

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Some Important Points Answered in this Market Report Are Given Below:

  • Explains an overview of the product portfolio, including product development, planning, and positioning.
  • Explains details about key operational strategies with a focus on R&D strategies, corporate structure, localization strategies, production capabilities, and financial performance of various companies.
  • Detailed analysis of the market revenue over the forecasted period.
  • Examining various outlooks of the market with the help of Porter’s five forces analysis, PEST & SWOT Analysis.
  • Study on the segments that are anticipated to dominate the market.
  • Study on the regional analysis that is expected to register the highest growth over the forecast period.

Key Topics Covered

  1. Introduction
  • Study Deliverables
  • Study Assumptions
  • Scope of the Study
  1. Research Methodology
  2. Executive Summary
  • Opportunity Map Analysis
  • Market at Glance
  • Market Share (%) and BPS Analysis, by Region
  • Competitive Landscape
  • Heat Map Analysis 
  • Market Presence and Specificity Analysis
  1. Investment Analysis
  2. Competitive Analysis

 

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